In May 2024, Ionis published the ATTUNE study protocol on clinicaltrials.gov.
With the aim of providing a better understanding to all, our team shortly after launched a global survey to collect questions about the study from families. We received over 150 questions from families across 18 countries. The questions were all addressed by MDS experts, including David Covini (DupMECP2), Katie Wester-Neal (MECP2 Duplication Foundation), Dr. Davut Pehlivan (NRI Houston), and Ionis’ team, ensuring every response is accurate.
This e-booklet compiles the answers to the most frequent questions and concerns from families worldwide.
These Q/A have been categorized into three main sections:
- Trial Logistics, Procedures, and Communication
- Drug-Related Questions
- Participants eligibility and selection
The content of this e-book is also the foundation for our two-part webinar series available on YouTube, providing another alternative format for families to obtain essential information.
Don’t hesitate to contact us if you still have questions.