{"id":33487,"date":"2025-05-20T14:00:00","date_gmt":"2025-05-20T12:00:00","guid":{"rendered":"https:\/\/dupmecp2.eu\/?p=33487"},"modified":"2025-09-10T08:37:22","modified_gmt":"2025-09-10T06:37:22","slug":"resultados-preliminares-hero","status":"publish","type":"post","link":"https:\/\/dupmecp2.eu\/es\/resultados-preliminares-hero\/","title":{"rendered":"Prometedores resultados preliminares del ensayo HERO para el s\u00edndrome"},"content":{"rendered":"<p>A principios de a\u00f1o, Alvin Luk particip\u00f3 en la <em>Medicina CRISPR<\/em> en Copenhague para ofrecer informaci\u00f3n actualizada sobre el ensayo cl\u00ednico HERO para el s\u00edndrome de duplicaci\u00f3n del gen MECP2. Su presentaci\u00f3n est\u00e1 a disposici\u00f3n de la comunidad en YouTube.<\/p>\n\n\n\n<p>En este v\u00eddeo, descubrir\u00e1 la terapia experimental CRISPR-Cas13 de Huidagene, <strong>HG204<\/strong>y la evoluci\u00f3n del primer ni\u00f1o tratado, tres meses despu\u00e9s de recibir el medicamento experimental. Nos vemos en el <strong>minuto 26:00<\/strong> para ver im\u00e1genes del paciente.<\/p>\n\n\n\n<p>Estos resultados iniciales son muy alentadores y sugieren una vez m\u00e1s que restaurar los niveles de prote\u00edna MeCP2 podr\u00eda ser una estrategia prometedora para combatir el s\u00edndrome.<\/p>\n\n\n\n<figure class=\"wp-block-image size-large\"><img fetchpriority=\"high\" decoding=\"async\" width=\"1024\" height=\"560\" src=\"https:\/\/dupmecp2.eu\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1024x560.png\" alt=\"\" class=\"wp-image-33492\" srcset=\"https:\/\/dupmecp2.eu\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1024x560.png 1024w, https:\/\/dupmecp2.eu\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-300x164.png 300w, https:\/\/dupmecp2.eu\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-768x420.png 768w, https:\/\/dupmecp2.eu\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1536x841.png 1536w, https:\/\/dupmecp2.eu\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-18x10.png 18w, https:\/\/dupmecp2.eu\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025.png 1842w\" sizes=\"(max-width: 1024px) 100vw, 1024px\" \/><\/figure>\n\n\n\n<figure class=\"wp-block-gallery has-nested-images columns-default is-cropped wp-block-gallery-1 is-layout-flex wp-block-gallery-is-layout-flex\">\n<figure class=\"wp-block-image size-large\"><img decoding=\"async\" width=\"1024\" height=\"576\" data-id=\"33489\" data-src=\"https:\/\/dupmecp2.eu\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-4-1024x576.png\" alt=\"\" class=\"wp-image-33489 lazyload\" data-srcset=\"https:\/\/dupmecp2.eu\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-4-1024x576.png 1024w, https:\/\/dupmecp2.eu\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-4-300x169.png 300w, https:\/\/dupmecp2.eu\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-4-768x432.png 768w, https:\/\/dupmecp2.eu\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-4-1536x864.png 1536w, https:\/\/dupmecp2.eu\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-4-18x10.png 18w, https:\/\/dupmecp2.eu\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-4.png 2008w\" data-sizes=\"(max-width: 1024px) 100vw, 1024px\" src=\"data:image\/svg+xml;base64,PHN2ZyB3aWR0aD0iMSIgaGVpZ2h0PSIxIiB4bWxucz0iaHR0cDovL3d3dy53My5vcmcvMjAwMC9zdmciPjwvc3ZnPg==\" style=\"--smush-placeholder-width: 1024px; --smush-placeholder-aspect-ratio: 1024\/576;\" \/><\/figure>\n\n\n\n<figure class=\"wp-block-image size-large\"><img decoding=\"async\" width=\"1024\" height=\"575\" data-id=\"33490\" data-src=\"https:\/\/dupmecp2.eu\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1-1024x575.png\" alt=\"\" class=\"wp-image-33490 lazyload\" data-srcset=\"https:\/\/dupmecp2.eu\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1-1024x575.png 1024w, https:\/\/dupmecp2.eu\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1-300x168.png 300w, https:\/\/dupmecp2.eu\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1-768x431.png 768w, https:\/\/dupmecp2.eu\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1.png 2006w\" data-sizes=\"(max-width: 1024px) 100vw, 1024px\" src=\"data:image\/svg+xml;base64,PHN2ZyB3aWR0aD0iMSIgaGVpZ2h0PSIxIiB4bWxucz0iaHR0cDovL3d3dy53My5vcmcvMjAwMC9zdmciPjwvc3ZnPg==\" style=\"--smush-placeholder-width: 1024px; --smush-placeholder-aspect-ratio: 1024\/575;\" \/><\/figure>\n\n\n\n<figure class=\"wp-block-image size-large\"><img decoding=\"async\" width=\"1024\" height=\"576\" data-id=\"33491\" data-src=\"https:\/\/dupmecp2.eu\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-3-1024x576.png\" alt=\"\" class=\"wp-image-33491 lazyload\" data-srcset=\"https:\/\/dupmecp2.eu\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-3-1024x576.png 1024w, https:\/\/dupmecp2.eu\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-3-300x169.png 300w, https:\/\/dupmecp2.eu\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-3-768x432.png 768w, https:\/\/dupmecp2.eu\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-3-1536x864.png 1536w, https:\/\/dupmecp2.eu\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-3-18x10.png 18w, https:\/\/dupmecp2.eu\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-3.png 2007w\" data-sizes=\"(max-width: 1024px) 100vw, 1024px\" src=\"data:image\/svg+xml;base64,PHN2ZyB3aWR0aD0iMSIgaGVpZ2h0PSIxIiB4bWxucz0iaHR0cDovL3d3dy53My5vcmcvMjAwMC9zdmciPjwvc3ZnPg==\" style=\"--smush-placeholder-width: 1024px; --smush-placeholder-aspect-ratio: 1024\/576;\" \/><\/figure>\n<\/figure>\n\n\n\n<p>Un segundo ni\u00f1o ya ha sido tratado con HG204, y se espera incluir sucesivamente hasta seis pacientes en este ensayo en China.<\/p>\n\n\n\n<div class=\"wp-block-buttons is-layout-flex wp-block-buttons-is-layout-flex\">\n<div class=\"wp-block-button\"><a class=\"wp-block-button__link has-white-color has-text-color has-background has-link-color wp-element-button\" href=\"https:\/\/www.youtube.com\/watch?v=uVFNm1UWQv8\" style=\"border-radius:11px;background-color:#f7a13f\">Ir al v\u00eddeo<\/a><\/div>\n<\/div>","protected":false},"excerpt":{"rendered":"<p>Plus t\u00f4t cette ann\u00e9e, Alvin Luk a particip\u00e9 \u00e0 la conf\u00e9rence CRISPR Medicine \u00e0 Copenhagen afin de pr\u00e9senter les nouveaut\u00e9s sur l\u2019essai clinique HERO pour le syndrome de duplication du [&hellip;]<\/p>","protected":false},"author":1,"featured_media":33493,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[7,201],"tags":[],"class_list":["post-33487","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-actualite","category-recherche-fr"],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v25.8 - https:\/\/yoast.com\/wordpress\/plugins\/seo\/ -->\n<title>R\u00e9sultats pr\u00e9liminaires prometteurs de l\u2019essai HERO pour le syndrome - DupMECP2<\/title>\n<meta name=\"description\" content=\"Plus t\u00f4t cette ann\u00e9e, Alvin Luk a particip\u00e9 \u00e0 la conf\u00e9rence CRISPR Medicine \u00e0 Copenhagen afin de pr\u00e9senter les nouveaut\u00e9s sur l\u2019essai clinique HERO pour le syndrome de duplication du g\u00e8ne MECP2. Sa pr\u00e9sentation est disponible sur YouTube pour la communaut\u00e9.\" \/>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/dupmecp2.eu\/es\/resultados-preliminares-hero\/\" \/>\n<meta property=\"og:locale\" content=\"es_ES\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"R\u00e9sultats pr\u00e9liminaires prometteurs de l\u2019essai HERO pour le syndrome - DupMECP2\" \/>\n<meta property=\"og:description\" content=\"Plus t\u00f4t cette ann\u00e9e, Alvin Luk a particip\u00e9 \u00e0 la conf\u00e9rence CRISPR Medicine \u00e0 Copenhagen afin de pr\u00e9senter les nouveaut\u00e9s sur l\u2019essai clinique HERO pour le syndrome de duplication du g\u00e8ne MECP2. 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